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Issue Date
Title
Author(s)
2007
Mutational analysis of mucopolysaccharidosis type VI patients undergoing a phase II trial of enzyme replacement therapy
Karageorgos, L.
;
Brooks, D.
;
Harmatz, P.
;
Ketteridge, D.
;
Pollard, A.
;
Melville, E.
;
Parkinson-Lawrence, E.
;
Clements, P.
;
Hopwood, J.
2005
An index case for the attenuated end of the mucopolysaccharidosis type VI clinical spectrum
Brooks, D.
;
Gibson, G.
;
Karageorgos, L.
;
Hein, L.
;
Robertson, E.
;
Hopwood, J.
2012
Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats
Ponder, K.
;
O'Malley, T.
;
Wang, P.
;
O'Donnell, P.
;
Traas, A.
;
Knox, V.
;
Aguirre, G.
;
Ellinwood, N.
;
Metcalf, J.
;
Wang, B.
;
Parkinson-Lawrence, E.
;
Sleeper, M.
;
Brooks, D.
;
Hopwood, J.
;
Haskins, M.
1995
In vivo delivery of human α-L-iduronidase in mice implanted with neo-organs
Salvetti, A.
;
Moullier, P.
;
Cornet, V.
;
Brooks, D.
;
Hopwood, J.
;
Danos, O.
;
Heard, J.M.
Discover
Author
2
Karageorgos, L.
2
Parkinson-Lawrence, E.
1
Aguirre, G.
1
Clements, P.
1
Cornet, V.
1
Danos, O.
1
Ellinwood, N.
1
Gibson, G.
1
Harmatz, P.
1
Haskins, M.
.
next >
Subject
3
Humans
3
N-Acetylgalactosamine-4-Sulfatase
2
Adult
2
Animals
2
DNA Mutational Analysis
2
Genetic Vectors
2
Male
2
Mucopolysaccharidosis VI
1
Adolescent
1
Animals, Newborn
.
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Date issued
1
2010 - 2012
2
2000 - 2009
1
1995 - 1999